Fore One Purpose Builds Community for Rare Disease

The Andelyn Foundation's annual Fore One Purpose golf tournament raised funds to support gene therapy treatment for children with nonketotic hyperglycinemia (NKH), a rare genetic disorder. This year, the event helped fund a clinical trial for two siblings, Drake and Vivian O’Sullivan, offering hope for a potential cure that could benefit a larger portion of the NKH population. The foundation aims to expand its support for families battling rare diseases through further clinical trials and community outreach.

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تنويه: هذا ملخص تم إنشاؤه بواسطة الذكاء الاصطناعي

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